Recent Posts
- FDA sees no need for DCCR advisory committee meeting
- Soleno’s DCCR under FDA priority review for hyperphagia in PWS
- CSTI-500 earns FDA’s rare pediatric disease designation for PWS
- Soleno files for US approval of DCCR for hyperphagia
- Seizures more likely in PWS caused by genetic deletion mutations
- PWS Awareness Month in May shines spotlight on the rare genetic disease
- Pitolisant enters pivotal Phase 3 testing for daytime sleepiness in PWS
- Pitolisant earns FDA orphan drug status ahead of Phase 3 trial
- Some PWS symptoms are more common with genetic deletion mutations: Study
- Tool to capture food-seeking behaviors in PWS clinical trials works in real life, too