• Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic
  • Saniona Planning Phase 2b Trial of Tesomet in Controlling Hunger
  • DCCR Fails to Reduce Excessive Appetite But Improves Other Measures, Data Show
  • Lack of Vitamin D in Diet Linked to Lower Levels in PWS Patients in Study
  • Coalition Will Address Racial Disparities in Rare Disease Communities
  • Tracking Eye Movements Can Measure Chronic Desire to Overeat
  • Liraglutide Helped Maintain Rapid Weight Loss in Teenager With PWS
  • COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say
  • Researchers Find Corticol Deficiency Rare in PWS, Advise Against Routine Hydrocortisone Use
  • Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe
  • Video Games Connect Chronically Ill Children Isolated at Home, Hospital
  • Unity and EU-wide Efforts Focus of Online Rare Disease Meeting