An ongoing, global clinical trial testing Aardvark Therapeutics’ ARD-101 for hyperphagia, or excessive hunger, in people with Prader-Willi syndrome (PWS) has lowered the minimum enrollment age in the U.S. to allow children as young as 7 to take part, according to a study update. The Phase 3…
Discussion
February has two different meanings for our family. On one hand, it’s the month of roses, chocolates, cards, and heart-shaped everything. On the other, it’s Rare Disease Awareness Month, culminating in Rare Disease Day on Feb. 28. It’s a time when families like ours, who are living with…
Non-obese children with Prader-Willi syndrome (PWS) have imbalances in the blood levels of signaling molecules that facilitate communication between muscles, bones, and fat tissue, a single-center study from Poland suggests. According to the researchers, such imbalances “may impair muscle development and bone metabolism” in “normal-weight children” with the rare…
Prader-Will syndrome is a rare and complex genetic condition that results in a variety of physical and mental symptoms. Learn more about the disease here.
Prader-Willi is caused by genetic changes in a particular area of chromosome 15. Learn more about what causes the disease here.
Symptoms of Prader-Willi range from physical impairments to cognitive and behavioral issues. Learn more about the symptoms of the disease here.
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