Specific genetic subtypes and growth hormone use both influence the physical characteristics, such as head shape and eye appearance, of…
Articles by Marisa Horak, MS
Soleno Therapeutics has partnered with Vanderbilt University to develop therapies that work as ATP-dependent potassium channel activators for rare diseases,…
Tonix Pharmaceuticals has licensed technology from the French National Institute of Health and Medical Research (Inserm) that it…
Inversago Pharma‘s INV-101 has been granted rare pediatric disease (RPD) designation by the U.S. Food and Drug Administration for…
The National Organization for Rare Disorders (NORD)’s RareLaunch training program will host two days of free virtual workshops…
A majority of rare disease patients using telehealth during the COVID-19 pandemic thought the experience positive, and many would like…
Measuring how electricity moves through the body could help detect low-grade inflammation in adults with Prader-Willi syndrome (PWS) without…
Severe fluid and calorie restriction induced rapid weight loss that was effectively maintained with liraglutide, according to a…
The Foundation for Prader-Willi Research (FPWR) is funding nine projects that intend to improve understanding and help find treatments,…
Levels of the hormone irisin are elevated in obese people, but not in those with Prader-Willi syndrome (PWS),…