• Rare Disease Day ‘Patient Hero’ Raises Awareness Through Fashion
  • Soleno Looking to Expand Potential Therapies That Work Like DCCR
  • PWS Subtypes May Respond Differently to Psychotropic Treatments
  • Rare Disease Day at NIH, Set for March 1, Growing Year by Year
  • Eurordis Survey: Healthcare Experience Worse for Rare Disease Patients
  • Growth Hormone Therapy Also Benefits Adults, IPWSO Argues
  • Tonix Licenses Via-the-nose Treatment Technology From Inserm
  • Tryp Therapeutics Readies First Trial of TRP-8802 for Excessive Appetite
  • Pandemic Won’t Stop Rare Disease Day on Feb. 28
  • COVID-19 Pandemic ‘Significantly’ Affected DCCR Phase 3 Trial, Soleno Says
  • Antidepressant Sertraline May Help Control Temper Outbursts
  • NORD’s 6th ‘State Report Card’ Notes Progress, Raises Concerns