News

FDA Grants Fast Track Status to Soleno’s Investigational Therapy DCCR for PWS

Soleno Therapeutics recently received fast track status from the U.S. Food and Drug Administration for diazoxide choline controlled-release (DCCR), its investigational treatment for Prader-Willi syndrome (PWS). DCCR is an extended-release, salt formulation of diazoxide, taken as a once-daily tablet. Diazoxide is a potassium channel activator, capable of crossing…

Inversago Raises $7M to Develop New Cannabinoid-1 Receptor Blockers

Inversago Pharma has raised $7 million to support the development of a new generation of cannabinoid-1 (CB1) receptor blockers for the treatment of Prader-Willi syndrome, type 1 diabetes, and other metabolic disorders. With the money, Inversago plans to advance its new compounds into clinical trials. CB1 inhibitors have…

PATH for PWS, a Prader-Willi Study, to Start Enrolling Patients in September

Zafgen biopharma and the nonprofit Foundation for Prader-Willi Research (FPWR) have launched “PATH for PWS,” a natural history study aimed at advancing the understanding of the medical history and medical events in patients with Prader-Willi syndrome (PWS). The non-interventional, observational study aims to document serious medical events experienced by Prader-Willi patients…